Description |
1 online resource (xxiv, 191 pages) : color illustrations |
Note |
Online resource; title from PDF title page (EBSCO, viewed July 23, 2015) |
Bibliography |
Includes bibliographical references and index. |
Contents |
Introduction to muscular dystrophy / Raymond A. Huml -- Muscular dystrophy : historical background and types / Raymond A. Huml -- FSHD : the most common type of muscular dystrophy? / Raymond A. Huml and Daniel P. Perez -- Duchenne and Becker muscular dystrophies : underlying genetic and molecular mechanisms / Jean K. Mah -- An overview of the other muscular dystrophies : underlying genetic and molecular mechanisms / Jean K. Mah -- Transition from childhood to adult in patients with muscular dystrophy / Elba Yesi Gerena Maldonado and Kathryn R. Wagner -- Overview of current treatments for muscular dystrophy / Zheng (Jane) Fan -- Physical therapy and orthotic devices / Laura E. Case -- Orthopedic management of the child with muscular dystrophy / Robert K. Lark and Elizabeth W. Hubbard -- Global regulatory landscape / Raymond A. Huml -- Key challenges to the approval of products to treat patients with muscular dystrophy / Raymond A. Huml -- Pharmaceutical products and non-pharmaceutical interventions as potential treatments for patients with muscular dystrophy / Raymond A. Huml -- US patient advocacy groups / Meredith L. Huml -- Global and national patient registries / Raymond A. Huml -- Summary / Raymond A. Huml. |
Summary |
This practical and concise guide offers an overview of muscular dystrophy's (MD) complicated features, treatment options and general resources. New treatments and a greater understanding of proteins and structures associated with MD are discussed along with long-term patient care. Also included are clinical and developmental challenges within the current regulatory landscape and recent scientific and clinical advances. Muscular Dystrophy: A Concise Guide offers clinicians, researchers, pharmaceutical executives and patient advocacy groups an easy-to-read reference that provides the necessary perspectives of the care giver and patient. |
Subject |
Muscular dystrophy.
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Muscular dystrophy -- Diagnosis.
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Muscular dystrophy -- Treatment.
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HEALTH & FITNESS / Diseases / General
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MEDICAL / Clinical Medicine
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MEDICAL / Diseases
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MEDICAL / Evidence-Based Medicine
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MEDICAL / Internal Medicine
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Added Author |
Huml, Raymond A., editor.
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ISBN |
9783319173627 electronic bk. |
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3319173626 electronic bk. |
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